Spark Therapeutics


Spark Therapeutics, now fully integrated into the Roche Group, is dedicated to delivering innovative gene therapies to improve patients' lives. They focus on treatments like Luxturna® and provide resources for healthcare providers and patients. Their mission is to make a difference by improving lives and creating healthier communities.

Industries

biotechnology
genetics
medical
therapeutics

Nr. of Employees

large (251-1000)


Patents

Relative potency assay for viral vector encoding isomerohydrolases

US-12359239-B2

View Details

Optimized promoter sequences, intron-free expression constructs and methods of use

US-12290574-B2

View Details

Codon-optimized acid alpha-glucosidase expression cassettes and methods of using same

US-12084693-B2

View Details

Column-based fully scalable rAAV manufacturing process

US-11702639-B2

View Details

CpG reduced factor VIII variants, compositions and methods and uses for treatment of hemostasis disorders

US-11168124-B2

View Details

Rab Escort Protein potency assay

US-10633689-B2

View Details

Products

Gene therapy for inherited retinal disease (voretigene neparvovec-rzyl)

A prescription gene therapy product for a specified inherited retinal disease; prescribing information and additional product resources are provided via linked materials.


Services

Online submission channel to receive medical or clinical trial inquiries from healthcare providers.

Patient-facing resources and links to support programs for individuals receiving prescription therapies.

Guidance and contact information for reporting suspected adverse reactions and product complaints to regulatory authorities and to the company.

Provision of official prescribing information and downloadable product labeling for prescription medicines.

Expertise Areas

  • Gene therapy development and commercialization
  • Pharmacovigilance and safety reporting
  • Medical information services for healthcare providers
  • Patient support and medicine information
  • Show More (1)

Key Technologies

  • Gene therapy
  • Pharmacovigilance reporting systems
  • Medical information management

Similar organizations

Browse all ORGANIZATIONS

JOIN OUR MAILING LIST

Stay Connected with MTEC

Keep up with active and upcoming solicitations, MTEC news and other valuable information.