Akcea Therapeutics
Akcea Therapeutics is a development and commercialization company focused on helping patients with serious diseases. Our priority is to drive clinical program execution, understand patient and physician needs, prepare the market, create market access, and commercialize our products on a global basis. .
Industries
Nr. of Employees
medium (51-250)
Akcea Therapeutics
Cambridge, Massachusetts, United States, North America
Products
TEGSEDI™ (inotersen)
An antisense drug designed to decrease the amount of mutant and normal TTR made by the liver, aimed at reducing TTR deposits and slowing or stopping the progression of hereditary ATTR amyloidosis (hATTR).
Volanesorsen
A potential treatment for familial chylomicronemia syndrome (FCS) designed to reduce the production of a protein in the liver that regulates plasma triglycerides.
Antisense Technology
A drug discovery platform that targets RNA to treat illnesses where no other therapeutic approaches have proven effective or ever existed.
Genetic Medicines Development
The process of discovering, developing, and delivering medicines that target the root causes of serious and rare diseases.
TEGSEDI™ (inotersen)
An antisense drug designed to decrease the amount of mutant and normal TTR made by the liver, aimed at reducing TTR deposits and slowing or stopping the progression of hereditary ATTR amyloidosis (hATTR).
Volanesorsen
A potential treatment for familial chylomicronemia syndrome (FCS) designed to reduce the production of a protein in the liver that regulates plasma triglycerides.
Antisense Technology
A drug discovery platform that targets RNA to treat illnesses where no other therapeutic approaches have proven effective or ever existed.
Genetic Medicines Development
The process of discovering, developing, and delivering medicines that target the root causes of serious and rare diseases.