Achillion Pharmaceuticals, Inc.
Alexion is dedicated to transforming the lives of people affected by rare diseases through innovative medicines, research, and patient-centric approaches. As part of AstraZeneca, the company emphasizes patients first, science and innovation, and health equity to develop breakthrough therapies and improve outcomes for the rare disease community.
Industries
Nr. of Employees
medium (51-250)
Achillion Pharmaceuticals, Inc.
121 Seaport Blvd, Boston, MA 02210, USA
Patents
Aryl, heteroaryl, and heterocyclic compounds for treatment of immune and inflammatory disorders
US-12338230-B2
View DetailsAryl, heteroaryl, and heterocyclic pharmaceutical compounds for treatment of medical disorders
US-12162860-B2
View DetailsAryl, heteroaryl, and heterocyclic compounds for treatment of medical disorders
US-12139497-B2
View Details
Aryl, heteroaryl, and heterocyclic compounds for treatment of immune and inflammatory disorders
US-12338230-B2
View DetailsAryl, heteroaryl, and heterocyclic pharmaceutical compounds for treatment of medical disorders
US-12162860-B2
View DetailsAryl, heteroaryl, and heterocyclic compounds for treatment of medical disorders
US-12139497-B2
View DetailsProducts
Therapeutic pipeline for rare diseases
A diversified development portfolio and pipeline of therapeutic candidates across multiple modalities and therapeutic areas focused on rare diseases, used to support clinical development and regulatory submissions.
Therapeutic pipeline for rare diseases
A diversified development portfolio and pipeline of therapeutic candidates across multiple modalities and therapeutic areas focused on rare diseases, used to support clinical development and regulatory submissions.
Services
External partnership program to evaluate and collaborate on preclinical translation, target discovery, and technologies aligned to the company's therapeutic interests.
Processes and guidance for investigator-sponsored research and externally sponsored collaborations, including submission pathways and investigator obligations.
Grant programs supporting independent medical education and patient advocacy initiatives, and centralized review for grant funding decisions.
Operational patient support offerings including disease and treatment education, access support for insurance/navigation, ongoing support services, and community connection initiatives.
Design and execution of clinical trials for rare diseases, emphasizing patient-informed endpoints, recruitment and retention strategies, and regulatory compliance.
Assessment and administration of unsolicited requests for access to investigational medicines for patients who have exhausted other therapeutic options, subject to local law and supply considerations.
External partnership program to evaluate and collaborate on preclinical translation, target discovery, and technologies aligned to the company's therapeutic interests.
Processes and guidance for investigator-sponsored research and externally sponsored collaborations, including submission pathways and investigator obligations.
Grant programs supporting independent medical education and patient advocacy initiatives, and centralized review for grant funding decisions.
Operational patient support offerings including disease and treatment education, access support for insurance/navigation, ongoing support services, and community connection initiatives.
Design and execution of clinical trials for rare diseases, emphasizing patient-informed endpoints, recruitment and retention strategies, and regulatory compliance.
Assessment and administration of unsolicited requests for access to investigational medicines for patients who have exhausted other therapeutic options, subject to local law and supply considerations.
Expertise Areas
- Rare disease research and development
- Clinical trial management for rare diseases
- Patient-centric trial design and patient engagement
- Translational target identification and biomarker development
Key Technologies
- Data science and artificial intelligence
- Genomics and next-generation sequencing
- Diagnostics development
- Digital health technologies
News & Updates
Supporting Patients and Caregivers. Read more about driving health equity for the rare disease community.
Collectively, more than 400 million people around the world are living with a rare disease.
Our mission to transform lives through innovation and research.
An interview with Chathuri Daluwatte about her role in Alexion's R&D.
Efforts to support patients with amyloidosis.
Innovations to improve diagnosis times.
Supporting Patients and Caregivers. Read more about driving health equity for the rare disease community.
Collectively, more than 400 million people around the world are living with a rare disease.
Our mission to transform lives through innovation and research.
An interview with Chathuri Daluwatte about her role in Alexion's R&D.
Efforts to support patients with amyloidosis.
Innovations to improve diagnosis times.